Niemann-Pick B - RS - 5th infusion.
Descrição
Necroptosis in Niemann–Pick disease, type C1: a potential therapeutic target
Frontiers Expert opinion on patient journey, diagnosis and clinical monitoring in acid sphingomyelinase deficiency in Turkey: a pediatric metabolic disease specialist's perspective
Niemann-Pick B - RS - 5th infusion.
Frontiers Pre-clinical Mouse Models of Neurodegenerative Lysosomal Storage Diseases
(PDF) Niemann-Pick Disease: An Underdiagnosed Lysosomal Storage Disorder
Investigational New Drug (IND) - The Addi and Cassi Fund
PDF) Intrathecal 2-hydroxypropyl-β-cyclodextrin decreases neurological disease progression in Niemann-Pick disease, type C1: a non-randomised, open-label, phase 1-2 trial
Niemann-Pick Disease
New Treatment of Disease that Swells Organs Gives New Hope to 4-year-old Girl - International Niemann-Pick Disease Alliance (INPDA)
PDF) Novel first-dose adverse drug reactions during a phase I trial of olipudase alfa (recombinant human acid sphingomyelinase) in adults with Niemann–Pick disease type B (acid sphingomyelinase deficiency)
WO2019130230A1 - Heterocyclic amides as kinase inhibitors - Google Patents
Pulmonary Type B Niemann-Pick Disease Successfully Treated with Lung Transplantation
PDF) Changes in PCSK 9 and Apolipoprotein B100 in Niemann-Pick Disease After Enzyme Replacement Therapy with Olipudase Alfa
Long-term administration of intravenous Trappsol® Cyclo™ (HP-β-CD) results in clinical benefits and stabilization or slowing of disease progression in patients with Niemann-Pick disease type C1: Results of an international 48-week Phase I/II
Investigating the Mechanism of Cyclodextrins in the Treatment of Niemann‐ Pick Disease Type C Using Crosslinked 2‐Hydroxypropyl‐β‐cyclodextrin - Carradori - 2020 - Small - Wiley Online Library
de
por adulto (o preço varia de acordo com o tamanho do grupo)
